Sobi’s Sanofi-partnered Altuvoct (efanesoctocog alfa) has been recommended by the National Institute for Health and Care ...

Tremfya, Stelara and Darzalex have been recommended for ulcerative colitis, Crohn’s disease and multiple myeloma, ...

The Medicines and Healthcare products Regulatory Agency (MHRA) has approved Galderma’s Nemluvio (nemolizumab) to treat both ...

Discover how health economics can support successful Medical Device launch, proposition development, and market access. Join ...

Approximately one to two people per million worldwide are diagnosed with the ultra-rare kidney disease every year ...

The European Medicines Agency’s (EMA) human medicines committee has recommended Krystal Biotech’s Vyjuvek (beremagene ...

Real-time payments: US respondents place slightly higher importance on speed of payment to participants (87% US sites and 81% ...

The Top Pharma List rankings are compiled from GlobalData’s pharmaceutical revenue figures, which are based on prescription medicine sales, including generics drugs. Listed below are the charts and ...

Around the world, events are being held to mark Rare Disease Day (28 February 2025), with the aim of bringing attention to ...

To deliver treatments for rare diseases more quickly, companies share how they are adapting their launch strategies and ...

A study led by Queen Mary University of London has found 69 previously unidentified genetic determinants of rare diseases.