Learn how CASGEVY, the first NHS-approved CRISPR gene therapy, treats sickle cell disease through a revolutionary genetic ...

The Sickle Cell Awareness Foundation, a nonprofit based in South Jamaica, is hosting its third symposium on Friday, April 4.The Sickle Cell Symposium will be held at NYC Health + ...

Novo Nordisk's rare disease unit awaits Phase 3 data for etavopivat in sickle cell disease, aiming for 50% VOC reduction ...

The growing occurrence of genetic disorders like sickle cell anemia, cystic fibrosis, and muscular dystrophy is fueling the demand for gene therapy and genome editing solutions, as these approaches ...

Congress did not reauthorize the rare pediatric disease priority review program at the end of 2024. Advocates say the ripple ...

The “Black Family Wellness Expo” is being held on Saturday, March 15 at Columbus Public Library. The event by The Links ...

Pregnant women with sickle cell disease are at higher risk of complications and require close monitoring, a nationwide French ...

EDIT stock is down following the announcement of dismal fourth-quarter 2024 results as both earnings and revenues miss estimates.

Dr. Marty Makary, Trump's nominee for FDA Commissioner, breezed through his confirmation hearing despite tough questions from Democrats and Republicans.

Vertex Pharmaceuticals demonstrates resilience with robust CF franchise, new approvals, and diversification efforts. Read why ...

These bodily rhythms work together to enhance your wellbeing and make you healthiest when your activity lines up with Earth’s ...

Loyal Source Government Services remains the chief healthcare provider for migrants in border custody almost two years after ...