A 19-year-old with cystic fibrosis (CF) is aiming to run the London Marathon to raise money for charity and awareness for the ...

In two randomised phase 3 studies involving 480 participants aged 12 years and over, ivacaftor/tezacaftor/vanzacaftor was ...

The UK’s Medicines and Healthcare products Regulatory Agency (MHRA) has today approved Alyftrek (triple combination medicine ...

Vertex Pharmaceuticals (NasdaqGS:VRTX) announced that its cystic fibrosis treatment, ALYFTREK®, had received regulatory approval from the UK's MHRA, a significant milestone in expanding its market ...

In a cohort of nearly 300 pediatric patients with cystic fibrosis, food allergy was found in less than 4% of the population, ...

The genetic disorder cystic fibrosis is unique because it can cause both breathing and digestive problems. Some 40,000 people in the U.S. currently have it, "though this is likely an ...

About 99% of women with cystic fibrosis (CF) use contraception at least once during their fertile years, but unintended pregnancy is common.

What's considered excellent revenue growth depends on the industry. For pharmaceutical companies, especially those with a ...

Researchers trial inhalable gene therapy for cystic fibrosis, offering a potential breakthrough in treating the genetic lung ...

Sionna Therapeutics recently secured an initial public offering (IPO) of $191m on the Nasdaq stock exchange, signalling ...

Infants with cystic fibrosis lack crucial “beneficial bacteria” in their gut, according to new research. Scientists say this ...

Highlights,Sionna Therapeutics has received positive coverage from TD Cowen, Stifel Nicolaus, and Guggenheim.,The stock ...